Von Willebrand factor/factor VIII concentrates in the treatment of von Willebrand disease. 2009

Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
Servicio de Hematología y Hemoterapia, Complexo Hospitalario Universitario Juan Canalejo, Departamento de Medicina, Universidad de Santiago de Compostela, A Corunna, Spain. jbatlle@canalejo.org

Therapy for von Willebrand disease (VWD) aims to restore the hemostatic function conferred by von Willebrand factor (VWF), which facilitates platelet adhesion and aggregation, and serves to increase potentially low coagulation factor VIII (FVIII) in plasma. In patients unresponsive to desmopressin (DDAVP), the preferred treatment is with plasma-derived VWF-containing FVIII concentrates. Only a few of the available VWF/FVIII concentrates have been licensed for use in VWD based on prospective studies. The efficacy of VWF/FVIII concentrates depends on the content and quality of VWF and FVIII. Several studies have demonstrated the variability of the VWF contents, as well as the differences in the VWF multimer patterns (including the high molecular weight VWF multimers that are most effective in restoring hemostasis), among these concentrates. Treating physicians should be aware of these disparities and the potential clinical implications for patients with different VWD subtypes. Dosing has traditionally been calculated based on the FVIII content of the products, although dosing based on VWF functional activity [e.g., VWF ristocetin cofactor activity (VWF:RCo)] addresses the primary protein deficiency in VWD patients. Several clinical studies have demonstrated the efficacy of concentrates dosed according to VWF:RCo. Dosing is generally consistent across VWD subtypes, although patients with severe phenotypes or undergoing major procedures may require more infusions or longer treatment duration. Other considerations for the use of VWF-containing concentrates include laboratory monitoring of efficacy and safety issues such as thrombosis risk and thromboprophylaxis.

UI MeSH Term Description Entries
D010973 Platelet Adhesiveness The process whereby PLATELETS adhere to something other than platelets, e.g., COLLAGEN; BASEMENT MEMBRANE; MICROFIBRILS; or other "foreign" surfaces. Adhesiveness, Platelet,Adhesivenesses, Platelet,Platelet Adhesivenesses
D010974 Platelet Aggregation The attachment of PLATELETS to one another. This clumping together can be induced by a number of agents (e.g., THROMBIN; COLLAGEN) and is part of the mechanism leading to the formation of a THROMBUS. Aggregation, Platelet
D002986 Clinical Trials as Topic Works about pre-planned studies of the safety, efficacy, or optimum dosage schedule (if appropriate) of one or more diagnostic, therapeutic, or prophylactic drugs, devices, or techniques selected according to predetermined criteria of eligibility and observed for predefined evidence of favorable and unfavorable effects. This concept includes clinical trials conducted both in the U.S. and in other countries. Clinical Trial as Topic
D003894 Deamino Arginine Vasopressin A synthetic analog of the pituitary hormone, ARGININE VASOPRESSIN. Its action is mediated by the VASOPRESSIN receptor V2. It has prolonged antidiuretic activity, but little pressor effects. It also modulates levels of circulating FACTOR VIII and VON WILLEBRAND FACTOR. Desmopressin,Vasopressin, Deamino Arginine,1-Deamino-8-D-arginine Vasopressin,1-Desamino-8-arginine Vasopressin,Adiuretin,Adiuretin SD,Apo-Desmopressin,DDAVP,Desmogalen,Desmopressin Acetate,Desmopressin Monoacetate,Desmopressin Monoacetate, Trihydrate,Desmopressine Ferring,Desmospray,Desmotabs,Minirin,Minurin,Nocutil,Octim,Octostim,Acetate, Desmopressin,Arginine Vasopressin, Deamino,Ferring, Desmopressine,Monoacetate, Desmopressin,Monoacetate, Trihydrate Desmopressin,Trihydrate Desmopressin Monoacetate,Vasopressin, 1-Deamino-8-D-arginine,Vasopressin, 1-Desamino-8-arginine
D004338 Drug Combinations Single preparations containing two or more active agents, for the purpose of their concurrent administration as a fixed dose mixture. Drug Combination,Combination, Drug,Combinations, Drug
D005169 Factor VIII Factor VIII of blood coagulation. Antihemophilic factor that is part of the factor VIII/von Willebrand factor complex. Factor VIII is produced in the liver and acts in the intrinsic pathway of blood coagulation. It serves as a cofactor in factor X activation and this action is markedly enhanced by small amounts of thrombin. Coagulation Factor VIII,Factor VIII Clotting Antigen,Factor VIII Coagulant Antigen,Factor VIII Procoagulant Activity,Thromboplastinogen,Blood Coagulation Factor VIII,F VIII-C,Factor 8,Factor 8 C,Factor Eight,Factor VIIIC,Hyate-C,Hyatt-C,F VIII C,Hyate C,HyateC,Hyatt C,HyattC
D006487 Hemostasis The process which spontaneously arrests the flow of BLOOD from vessels carrying blood under pressure. It is accomplished by contraction of the vessels, adhesion and aggregation of formed blood elements (eg. ERYTHROCYTE AGGREGATION), and the process of BLOOD COAGULATION. Hemostases
D006490 Hemostatics Agents acting to arrest the flow of blood. Absorbable hemostatics arrest bleeding either by the formation of an artificial clot or by providing a mechanical matrix that facilitates clotting when applied directly to the bleeding surface. These agents function more at the capillary level and are not effective at stemming arterial or venous bleeding under any significant intravascular pressure. Antihemorrhagic,Hemostatic,Antihemorrhagics
D006801 Humans Members of the species Homo sapiens. Homo sapiens,Man (Taxonomy),Human,Man, Modern,Modern Man
D013927 Thrombosis Formation and development of a thrombus or blood clot in BLOOD VESSELS. Atherothrombosis,Thrombus,Blood Clot,Blood Clots,Thromboses

Related Publications

Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
January 1998, Haemophilia : the official journal of the World Federation of Hemophilia,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
May 1999, Haemophilia : the official journal of the World Federation of Hemophilia,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
May 1989, American journal of hematology,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
January 2009, Transfusion medicine and hemotherapy : offizielles Organ der Deutschen Gesellschaft fur Transfusionsmedizin und Immunhamatologie,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
January 1980, American journal of hematology,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
September 2006, Seminars in thrombosis and hemostasis,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
January 2016, Therapeutics and clinical risk management,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
March 2009, Expert opinion on drug safety,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
April 2010, Blood coagulation & fibrinolysis : an international journal in haemostasis and thrombosis,
Javier Batlle, and María Fernanda López-Fernández, and Esther Lourés Fraga, and Angela Rodríguez Trillo, and María Almudena Pérez-Rodríguez
April 2005, Blood coagulation & fibrinolysis : an international journal in haemostasis and thrombosis,
Copied contents to your clipboard!