Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia. 2018

Ding An, and Jessica L Schneller, and Andrea Frassetto, and Shi Liang, and Xuling Zhu, and Ji-Sun Park, and Matt Theisen, and Sue-Jean Hong, and Jenny Zhou, and Raj Rajendran, and Becca Levy, and Rebecca Howell, and Gilles Besin, and Vladimir Presnyak, and Staci Sabnis, and Kerry E Murphy-Benenato, and E Sathyajith Kumarasinghe, and Timothy Salerno, and Cosmin Mihai, and Christine M Lukacs, and Randy J Chandler, and Lin T Guey, and Charles P Venditti, and Paolo G V Martini

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