Current and Future Perspective in Hematopoietic Stem Progenitor Cell-gene Therapy for Inborn Errors of Metabolism. 2023

Francesca Tucci, and Giulia Consiglieri, and Matilde Cossutta, and Maria Ester Bernardo
Pediatric Immunohematology and Bone Marrow Transplantation, IRCCS San Raffaele Scientific Institute, Milan, Italy.

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